- FDA Approves First Gene Therapy for Children with Metachromatic Leukodystrophy FDA.gov
- FDA approved a lifesaving therapy for children with a rare genetic disease. It might become the world’s most expensive drug CNN
- After Kyowa Kirin buyout, Orchard scores FDA approval for first MLD gene therapy in the US FiercePharma
- Orchard’s therapy for neuron disease in children wins FDA approval STAT
- Orchard Therapeutics Receives FDA Approval of Lenmeldy™ (atidarsagene autotemcel), the Only Therapy for Eligible Children with Early-onset Metachromatic Leukodystrophy in the U.S. GlobeNewswire
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